1. Myozyme 2. Lumizyme
For: Glycogen Storage Disease, Type II
Abecma
For: Multiple Myeloma
Actemra
For: Systemic Sclerosis
Actimmune
For: Chronic Granulomatous Disease
Adcetris
For: Mycosis Fungoides
Adcirca
For: Pulmonary Arterial Hypertension
Adempas
For: Chronic Thromboembolic Pulmonary Hypertension, Pulmonary Arterial Hypertension
Agamree
For: Duchenne Muscular Dystrophy
Agrylin
For: Essential Thrombocythemia
Albenza
For: Neurocysticercosis
Alimta
For: Malignant Pleural Mesothelioma
ALIQOPA
For: Follicular Lymphoma
Alomide Ophthalmic Solution
For: Vernal Keratoconjunctivitis
Alyftrek
For: Cystic Fibrosis
AmBisome
For: Cryptococcal Meningitis, Visceral Leishmaniasis
Amondys 45
For: Duchenne Muscular Dystrophy
Aqneursa
For: Niemann-Pick Disease, Type C
Aqvesme
For: Thalassemia
ARZERRA
For: B-Cell Chronic Lymphocytic Leukemia
Avastin
For: Malignant Glioma, Primary Peritoneal Carcinoma, Renal Cell Carcinoma
Avlayah
For: Mucopolysaccharidosis, MPS-II
Avonex
For: Multiple sclerosis
Ayvakit
For: Mastocytosis
BabyBIG
For: Infant Botulism
Banzel
For: Lennox-Gastaut Syndrome
Bavencio
For: Cutaneous Neuroendocrine Carcinoma
Bendeka
For: B-Cell Chronic Lymphocytic Leukemia
Beqalzi
For: Mantle Cell Lymphoma
Besponsa
For: B-Cell Acute Lymphoblastic Leukemia
Betaseron
For: Multiple sclerosis
Bizengri
For: Cholangiocarcinoma
BLENREP
For: Multiple Myeloma
Blenrep
For: Multiple Myeloma
Blincyto
For: Acute Lymphoid Leukemia
Bosulif
For: Chronic Myelogenous Leukemia, BCR-ABL1 Positive
Breyanzi
For: B-Cell Chronic Lymphocytic Leukemia, Mantle Cell Lymphoma, Primary Mediastinal Large B-Cell Lymphoma
Brineura
For: Neuronal Ceroid Lipofuscinosis 2
BRUKINSA
For: Mantle Cell Lymphoma
Brukinsa
For: B-Cell Chronic Lymphocytic Leukemia, Follicular Lymphoma
Bylvay
For: Progressive Familial Intrahepatic Cholestasis
CABLIVI
For: Thrombotic Thrombocytopenic Purpura
Cablivi
For: Thrombotic Thrombocytopenic Purpura
CABOMETYX
For: Hepatocellular Carcinoma
Cafcit
For: Apnea Of Prematurity
CALQUENCE
For: Mantle Cell Lymphoma
Calquence
For: Mantle Cell Lymphoma
Campath
For: B-Cell Chronic Lymphocytic Leukemia
Casgevy
For: Beta Thalassemia
Cavhanza
For: Chronic Myelogenous Leukemia, BCR-ABL1 Positive
Cayston
For: Cystic Fibrosis
Chemet capsules
For: Lead Poisoning
Colazal
For: Ulcerative colitis
Colcrys
For: Familial Mediterranean Fever
Copaxone
For: Multiple sclerosis
COPIKTRA
For: Follicular Lymphoma
Crenessity
For: Congenital Adrenal Hyperplasia
Cresemba
For: Invasive Aspergillosis, Zygomycosis
CYRAMZA
For: Gastric Cancer, Hepatocellular Carcinoma
Cystadane
For: Homocystinuria
Cystagon
For: Nephropathic Cystinosis
Cytovene
For: Cytomegalovirus Retinitis
DANYELZA
For: Neuroblastoma
Danziten
For: Chronic Myelogenous Leukemia, BCR-ABL1 Positive
Darzalex
For: Multiple Myeloma
Daybue
For: Rett Syndrome
Daybue Stix
For: Rett Syndrome
Defitelio
For: Hepatic Veno-Occlusive Disease
Doxil
For: Multiple Myeloma
Dupixent
For: Bullous Pemphigoid, Eosinophilic Esophagitis
EBANGA
For: Ebola Hemorrhagic Fever
Elevidys
For: Duchenne Muscular Dystrophy
Elmiron
For: Interstitial Cystitis
Elrexfio
For: Multiple Myeloma
Emflaza
For: Duchenne Muscular Dystrophy
Empaveli
For: Paroxysmal Nocturnal Hemoglobinuria
Empliciti
For: Multiple Myeloma
Enjaymo
For: Autoimmune Hemolytic Anemia
Eohilia
For: Eosinophilic Esophagitis
EPIDIOLEX
For: Lennox-Gastaut Syndrome
Epidiolex
For: Lennox-Gastaut Syndrome
Epkinly
For: Follicular Lymphoma
Epogen
For: Anemia
Erwinase
For: Acute Lymphoid Leukemia
ESBRIET
For: Idiopathic Pulmonary Fibrosis
Evkeeza
For: Homozygous Familial Hypercholesterolemia
Evrysdi
For: Spinal Muscular Atrophy
Exondys 51
For: Duchenne Muscular Dystrophy
Eylea
For: Retinopathy Of Prematurity
Fabhalta
For: Paroxysmal Nocturnal Hemoglobinuria
Farydak
For: Multiple Myeloma
Fasenra
For: Eosinophilic Granulomatosis With Polyangiitis, Hypereosinophilic Syndrome
Felbatol
For: Lennox-Gastaut Syndrome
Filspari
For: Focal Segmental Glomerulosclerosis
Filsuvez
For: Epidermolysis Bullosa
Fintepla
For: Lennox-Gastaut Syndrome
Folotyn
For: T-Cell Lymphoma
GALAFOLD
For: Fabry Disease
Gamifant
For: Hemophagocytic Syndrome
Gammagard Liquid
For: Multifocal Motor Neuropathy
Gastrocrom
For: Mastocytosis
GATTEX
For: Short Bowel Syndrome
GAZYVA
For: B-Cell Chronic Lymphocytic Leukemia, Follicular Lymphoma
Genotropin
For: Prader-Willi Syndrome
Gleevec
For: Chronic Myelogenous Leukemia, BCR-ABL1 Positive, Dermatofibrosarcoma Protuberans
Gliadel
For: Malignant Glioma
Gralise
For: Postherpetic Neuralgia
Halaven
For: Soft Tissue Sarcoma
Harliku
For: Alkaptonuria
Hepcludex
For: Hepatitis D Virus Infection
Horizant
For: Postherpetic Neuralgia
Humira
For: Juvenile Idiopathic Arthritis, Ulcerative colitis
Idhifa
For: Acute Myeloid Leukemia
ILARIS
For: Familial Mediterranean Fever
Imaavy
For: Myasthenia Gravis
Imbruvica
For: Chronic Graft Versus Host Disease, Mantle Cell Lymphoma, Splenic Marginal Zone Lymphoma
IMBRUVICA
For: B-Cell Chronic Lymphocytic Leukemia
Imcivree
For: Bardet-Biedl Syndrome
Imfinzi
For: Biliary Tract Cancer, Hepatocellular Carcinoma
Imjudo
For: Hepatocellular Carcinoma
IMPAVIDO
For: Leishmaniasis
Increlex
For: Growth Hormone Insensitivity Syndrome
Ingrezza
For: Huntington Disease
Inqovi
For: Acute Myeloid Leukemia
Iqirvo
For: Primary Biliary Cholangitis
Itvisma
For: Spinal Muscular Atrophy
Iwilfin
For: Neuroblastoma
JAKAFI
For: Graft Versus Host Disease
Jakafi
For: Graft Versus Host Disease, Myelofibrosis
Jakafi XR
For: Graft Versus Host Disease, Myelofibrosis
Jaypirca
For: Chronic Lymphocytic Leukemia/small Lymphocytic Lymphoma, Mantle Cell Lymphoma
Juxtapid
For: Homozygous Familial Hypercholesterolemia
Kalydeco
For: Cystic Fibrosis
Kanuma
For: Lysosomal Acid Lipase Deficiency
Keytruda
For: Carcinoma Of Esophagus, Cutaneous Neuroendocrine Carcinoma
Kimmtrak
For: Uveal Melanoma
Komzifti
For: Acute Myeloid Leukemia
Koselugo
For: Neurofibromatosis, Type 1
Krintafel
For: Malaria
Kymriah
For: Follicular Lymphoma
KYNAMRO
For: Homozygous Familial Hypercholesterolemia
Kyprolis
For: Multiple Myeloma
Lamictal
For: Lennox-Gastaut Syndrome
Lartruvo
For: Soft Tissue Sarcoma
LENVIMA
For: Hepatocellular Carcinoma
Letairis
For: Pulmonary Arterial Hypertension
Leukine
For: Acute Myeloid Leukemia
Leustatin Injection
For: Hairy Cell Leukemia
Lialda
For: Ulcerative colitis
Livdelzi
For: Primary Biliary Cholangitis
Livmarli
For: Progressive Familial Intrahepatic Cholestasis
Loqtorzi
For: Nasopharyngeal Carcinoma
LUMOXITI
For: Hairy Cell Leukemia
Lumryz
For: Narcolepsy
Lunsumio
For: Follicular Lymphoma
Lunsumio Velo
For: Follicular Lymphoma
Lupron Depot-Ped
For: Central Precocious Puberty
Lupron Injection
For: Central Precocious Puberty
Lynavoy
For: Primary Biliary Cholangitis
Lynozyfic
For: Multiple Myeloma
Lynparza
For: Fallopian Tube Cancer
Methotrexate
For: Bone Osteosarcoma
Miplyffa
For: Niemann-Pick Disease, Type C
Mobic
For: Juvenile Idiopathic Arthritis
Modeyso
For: Malignant Glioma
Monjuvi
For: Follicular Lymphoma
Mylotarg
For: Acute Myeloid Leukemia
Natpara
For: Hypoparathyroidism
NeoProfen
For: Patent Ductus Arteriosus
Nexavar
For: Hepatocellular Carcinoma, Renal Cell Carcinoma
Niktimvo
For: Chronic Graft Versus Host Disease
Ninlaro
For: Multiple Myeloma
Nipent
For: Hairy Cell Leukemia
Norditropin
For: Noonan Syndrome
NovoSeven
For: Congenital Factor VII Deficiency
Noxafil
For: Invasive Aspergillosis
Nplate
For: Autoimmune Thrombocytopenic Purpura
NUCALA
For: Eosinophilic Granulomatosis With Polyangiitis
NUCALA
For: Hypereosinophilic Syndrome
OCALIVA
For: Primary Biliary Cholangitis
Octagam 10%
For: Dermatomyositis
OFEV
For: Idiopathic Pulmonary Fibrosis
Ojemda
For: Malignant Glioma
Ojjaara
For: Myelofibrosis
Oncaspar; Asparlas
For: Acute Lymphoid Leukemia
Onfi
For: Lennox-Gastaut Syndrome
ONUREG
For: Acute Myeloid Leukemia
OPDIVO
For: Hepatocellular Carcinoma
Opdivo
For: Hepatocellular Carcinoma
Opsumit
For: Pulmonary Arterial Hypertension
Opsynvi
For: Pulmonary Arterial Hypertension
Opticrom 4% ophthalmic solution
For: Vernal Keratoconjunctivitis
Orencia
For: Graft Versus Host Disease
Orkambi
For: Cystic Fibrosis
Otarmeni
For: Hearing loss
Oxervate
For: Neurotrophic Keratopathy
Palsonify
For: Acromegaly
Papzimeos
For: Recurrent Respiratory Papillomatosis
PEMAZYRE
For: Cholangiocarcinoma
Phyrago
For: Chronic Myelogenous Leukemia, BCR-ABL1 Positive
Pomalyst
For: Multiple Myeloma
POMALYST
For: Kaposi Sarcoma
Praluent
For: Homozygous Familial Hypercholesterolemia
Pretomanid
For: Tuberculosis
Priftin
For: Pulmonary Tuberculosis
PROCYSBI
For: Cystinosis
Promacta
For: Aplastic Anemia
Pulmozyme
For: Cystic Fibrosis
Qalsody
For: Amyotrophic Lateral Sclerosis
Qutenza
For: Postherpetic Neuralgia
Radicava
For: Amyotrophic Lateral Sclerosis
Radicava ORS
For: Amyotrophic Lateral Sclerosis
REBETOL
For: Hepatitis C
Reblozyl
For: Myelodysplastic Syndrome
Redemplo
For: Familial Chylomicronemia Syndrome
Remicade
For: Crohn’s disease
Remodulin;Orenitram
For: Pulmonary Arterial Hypertension
Repatha
For: Homozygous Familial Hypercholesterolemia
Revlimid
For: Follicular Lymphoma, Mantle Cell Lymphoma, Multiple Myeloma
Revuforj
For: Acute Lymphoid Leukemia, Acute Myeloid Leukemia
Rezlidhia
For: Acute Myeloid Leukemia
Rilutek
For: Amyotrophic Lateral Sclerosis
Rituxan
For: B-Cell Chronic Lymphocytic Leukemia
Rituxan SC
For: Follicular Lymphoma
Rituxan(r); MabThera(r)
For: Pemphigus Vulgaris
Rivfloza
For: Primary Hyperoxaluria
Roferon A
For: Chronic Myelogenous Leukemia, BCR-ABL1 Positive
Rydapt
For: Acute Myeloid Leukemia, Mastocytosis
Ryoncil
For: Acute Graft Versus Host Disease
Rystiggo
For: Myasthenia Gravis
Rytelo
For: Myelodysplastic Syndrome
Sandostatin LAR
For: Acromegaly
Sarclisa
For: Multiple Myeloma
Sarclisa Escena
For: Multiple Myeloma
Scemblix
For: Chronic Myelogenous Leukemia, BCR-ABL1 Positive
Sensipar
For: Parathyroid Carcinoma
SIMPONI ARIA
For: Polyarticular Juvenile Idiopathic Arthritis
SIRTURO
For: Active Tuberculosis
Sirturo
For: Active Tuberculosis
Skysona
For: Adrenoleukodystrophy
Soliris
For: Atypical Hemolytic-Uremic Syndrome, Myasthenia Gravis, Neuromyelitis Optica
Somavert
For: Acromegaly
Spevigo
For: Generalized Pustular Psoriasis
Spinraza
For: Spinal Muscular Atrophy
Sprycel
For: Chronic Myelogenous Leukemia, BCR-ABL1 Positive
Stivarga
For: Hepatocellular Carcinoma
Strensiq
For: Hypophosphatasia
Sunosi
For: Narcolepsy
Supprelin Injection
For: Central Precocious Puberty
Supprelin LA
For: Central Precocious Puberty
Survanta intratracheal suspension
For: Respiratory Distress Syndrome In Premature Infants
Synarel Nasal Solution
For: Central Precocious Puberty
Synribo
For: Chronic Myelogenous Leukemia, BCR-ABL1 Positive
Talvey
For: Multiple Myeloma
Tasigna
For: Chronic Myelogenous Leukemia, BCR-ABL1 Positive
Tazverik
For: Follicular Lymphoma
TECARTUS
For: Mantle Cell Lymphoma
Tecelra
For: Soft Tissue Sarcoma
Tecentriq
For: Soft Tissue Sarcoma
Tecvayli
For: Multiple Myeloma
thalomid
For: Multiple Myeloma
Tibsovo
For: Cholangiocarcinoma
Topamax
For: Lennox-Gastaut Syndrome
Torisel
For: Renal Cell Carcinoma
Tracleer
For: Pulmonary Arterial Hypertension
Treanda
For: B-Cell Chronic Lymphocytic Leukemia
Trikafta
For: Cystic Fibrosis
Triptodur
For: Central Precocious Puberty
Trisenox
For: Acute Promyelocytic Leukemia
Truseltiq
For: Cholangiocarcinoma
Tryngolza
For: Familial Chylomicronemia Syndrome
Tyvaso
For: Pulmonary Arterial Hypertension
Tyvaso DPI
For: Pulmonary Arterial Hypertension
Ukoniq
For: Follicular Lymphoma, Splenic Marginal Zone Lymphoma
Ultomiris
For: Myasthenia Gravis, Neuromyelitis Optica, Paroxysmal Nocturnal Hemoglobinuria
Unituxin
For: Neuroblastoma
Uplizna
For: Myasthenia Gravis
Uptravi
For: Pulmonary Arterial Hypertension
URSO 250
For: Primary Biliary Cholangitis
Valchlor
For: Mycosis Fungoides
Vanflyta
For: Acute Myeloid Leukemia
Velcade
For: Mantle Cell Lymphoma, Multiple Myeloma
VENCLEXTA
For: Acute Myeloid Leukemia, B-Cell Chronic Lymphocytic Leukemia
Ventavis
For: Pulmonary Arterial Hypertension
Verkazia
For: Vernal Keratoconjunctivitis
Vesanoid
For: Acute Promyelocytic Leukemia
Vidaza
For: Juvenile Myelomonocytic Leukemia
VILTEPSO
For: Duchenne Muscular Dystrophy
Vitrasert Implant
For: Cytomegalovirus Retinitis
Voranigo
For: Glioma
Voxzogo
For: Achondroplasia
Voydeya
For: Paroxysmal Nocturnal Hemoglobinuria
VPRIV
For: Gaucher Disease
Vykat XR
For: Prader-Willi Syndrome
Vyloy
For: Gastric Cancer
Vyvgart
For: Myasthenia Gravis
Vyvgart Hytrulo
For: Myasthenia Gravis
VYXEOS ; Vyxeos ; Vyxeos
For: Acute Myeloid Leukemia
WAKIX
For: Narcolepsy
Wakix
For: Narcolepsy
WAKIX
For: Narcolepsy
Waskyra
For: Wiskott-Aldrich Syndrome
Winrevair
For: Pulmonary Arterial Hypertension
WinRho SD
For: Autoimmune Thrombocytopenic Purpura
Xalkori
For: Anaplastic Large Cell Lymphoma, Inflammatory Myofibroblastic Tumor
Xermelo
For: Carcinoid Syndrome
Xgeva
For: Giant Cell Tumor Of Bone
Xifaxan
For: Hepatic Encephalopathy
XPOVIO
For: Multiple Myeloma
Xpovio
For: Multiple Myeloma
Xyrem
For: Narcolepsy
Xywav
For: Idiopathic Hypersomnia, Narcolepsy
Yescarta
For: Follicular Lymphoma
Yondelis
For: Soft Tissue Sarcoma
Yorvipath
For: Hypoparathyroidism
Yuviwel
For: Achondroplasia
Zavesca
For: Gaucher Disease
Zelboraf
For: Erdheim-Chester Disease
Ziihera
For: Biliary Tract Cancer
Zilbrysq
For: Myasthenia Gravis
ZOLGENSMA
For: Spinal Muscular Atrophy
Zydelig
For: Follicular Lymphoma
Zynyz
For: Cutaneous Neuroendocrine Carcinoma
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